Gene therapy for mitochondrial disorders

JIMD Podcasts
25/10/2024 26 min
Gene therapy for mitochondrial disorders

Listen "Gene therapy for mitochondrial disorders"

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Episode Synopsis

Professor Shamima Rahman and Dr Nandaki Keshavan take us on a whistle stop tour of the different approaches taken to gene therapy in mitochondrial disease and why some may work better than others.

Gene therapy for mitochondrial disorders
Nandaki Keshavan, Michal Minczuk, Carlo Viscomi, Shamima Rahman
https://doi.org/10.1002/jimd.12699

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