TUESDAY, January 21, 2014 - 3:30 pm PST/6:30 pm EST Join us for a 3-part series on gene therapy for Huntington's disease. Our incredible special presenter is Benjamin E. Deverman, Ph.D. from California Institute of Technology who is going to give us some very interesting insight and education about what exactly is gene therapy. What are the goals of this therapy and what genes can be used for gene therapy in HD. What are inhibitory RNAs, ASOs and other therapeutic strategies like trophic factors? We will be learning how gene therapies are going to be delivered. What is AAV and "naked" DNA? We will hear about some encouraging results from clinical trials for other diseases and why they show promise for HD. Tune in for a very educational and informational show.

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