Neuronopathic gaucher disease

JIMD Podcasts
27/09/2024 25 min
Neuronopathic gaucher disease

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Episode Synopsis

Originally presented at the SSIEM 2023 Annual Symposium, Dr Ozlem Goker-Alpan discusses neuronopathic gaucher disease, regional variations and hopes for new treatments.

Neuronopathic Gaucher disease: Rare in the West, common in the East
Ozlem Goker-Alpan, Margarita M. Ivanova
https://doi.org/10.1002/jimd.12749

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