Gene therapy in urea cycle disorders: a historical perspective and future prospects

JIMD Podcasts
01/09/2023 11 min
Gene therapy in urea cycle disorders: a historical perspective and future prospects

Listen "Gene therapy in urea cycle disorders: a historical perspective and future prospects"

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Episode Synopsis

Dr Julien Baruteau joins the podcast to look back at the history of gene therapy research in Urea Cycle Disorders, and discuss the future of genomic therapies in this group of conditions with a high unmet need.

Gene therapy for urea cycle defects: An update from historical perspectives to future prospects
Claire Duff, et al
https://doi.org/10.1002/jimd.12609

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