How a custom-made gene therapy could save one baby's life

17/05/2025 4 min
How a custom-made gene therapy could save one baby's life

Listen "How a custom-made gene therapy could save one baby's life"

Episode Synopsis

A baby born with a rare, life-threatening genetic disease is now thriving after receiving an experimental gene-editing treatment. He's one of the first to be successfully treated with a bespoke therapy targeting a tiny but deadly error in his DNA. His doctors hope the technology could one day help the estimated 350 million people worldwide with rare diseases.

More episodes of the podcast Headlines on health