Genetic therapies in store for neurodevelopmental disorders

16/06/2025 44 min
Genetic therapies in store for neurodevelopmental disorders

Listen "Genetic therapies in store for neurodevelopmental disorders"

Episode Synopsis

Gene therapies have been in the news lately. They are being used to help individuals who have a genetic variant linked to a disorder or disease, including but not limited to: spinal muscular atrophy, carbamoyl phosphate synthetase 1 (CPS1) deficiency, diabetes and some types of cancers. What is the promise in rare genetic forms of … Continue reading "Genetic therapies in store for neurodevelopmental disorders"