Glitazones in X-linked adrenoleukodystrophy

JIMD Podcasts
22/07/2022 8 min
Glitazones in X-linked adrenoleukodystrophy

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Episode Synopsis

Dr Pierre-Axel Monternier discusses his group's work looking at a modified form of the drug pioglitazone to treat X-linked adrenaleukodystrophy.

Therapeutic potential of deuterium-stabilized (R)-pioglitazone—PXL065—for X-linked adrenoleukodystrophy
Pierre-Axel Monternier, et al
https://doi.org/10.1002/jimd.12510

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