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Listen "Genomic Therapies In IMD: Lessons from MMA"
Episode Synopsis
In this podcast, Dr Chuck Venditti of the National Human Genome Research Institute, discusses his passion for MMA, the role of screening and the mechanisms behind different types of genomic therapy.
Treatment of metabolic disorders using genomic technologies: Lessons from methylmalonic acidemia
Leah E. Venturoni and Charles P. Venditti
https://doi.org/10.1002/jimd.12534
Treatment of metabolic disorders using genomic technologies: Lessons from methylmalonic acidemia
Leah E. Venturoni and Charles P. Venditti
https://doi.org/10.1002/jimd.12534
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