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Listen "Gene therapy in Glycogen Storage Disorders"
Episode Synopsis
Dr Dwight Koeberl joins the podcast to provide some background to gene therapies in Glycogen Storage Disorders, hi-light some ongoing studies and explain why we owe at least some of our knowledge to a menagerie of animal models.
Gene therapy for glycogen storage diseases
Dwight D. Koeberl, et al
https://doi.org/10.1002/jimd.12654
Gene therapy for glycogen storage diseases
Dwight D. Koeberl, et al
https://doi.org/10.1002/jimd.12654
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