Listen "Chasing Cures"
Episode Synopsis
Many gene therapy companies seek to exploit a platform technology or leverage a specific vector. Rocket Pharmaceuticals is pursuing a multi-platform pipeline of treatments that directly target the genetic mutation underlying rare, childhood disorders. We spoke to Gaurav Shah, CEO of Rocket, about the companies approach to gene therapy, the conditions it’s targeting, and how it determines what gene therapies it will pursue.
More episodes of the podcast RARECast
Turning a Rare Cancer into a Call to Action
24/12/2025
Finding Strength in Weakness
11/12/2025
Navigating Your Child’s Rare Disease
20/11/2025
ZARZA We are Zarza, the prestigious firm behind major projects in information technology.